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Brambilla, Riccardo; Biffi, A.; Bordignon, C.; Naldini, L. (2004)
Languages: English
Types: Article
Subjects:
  • The results below are discovered through our pilot algorithms. Let us know how we are doing!

    • 1. Kolodney, E.H., and Fluharty, A.L. 1995. Metachromatic leukodystrophy and multiple sulfatase deficiency: sulfatide lipidosis. In The metabolic and molecular bases of inherited disease. 6th edition. C.R. Scriver, A.L. Beaudet, W.S. Sly, and D. Valle, editors. McGraw-Hill, New York, USA. 2693-7391.
    • 2. Neufeld, E.F. 1991. Lysosomal disease. Annu. Rev. Biochem. 60:257-280.
    • 3. Kay, M.A., Glorioso, J.C., and Naldini, L. 2001. Viral vectors for gene therapy: the art of turning infectious agents into vehicles of therapeutics. Nat. Med. 7:33-40.
    • 4. Glorioso, J.C., Mata, M., and Fink, D.J. 2003. Therapeutic gene transfer to the nervous system using viral vectors. J. Neurovirol. 9:165-172.
    • 5. Consiglio, A., et al. 2001. In vivo gene therapy of metachromatic leukodystrophy by lentiviral vectors: correction of neuropathology and protection against learning impairments in affected mice. Nat. Med. 7:310-316.
    • 6. Bosch, A., Perret, E., Desmaris, N., Trono, D., and Heard, J.M. 2000. Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer. Hum. Gene Ther. 11:1139-1150.
    • 7. Kordower, J.H., et al. 1999. Lentiviral gene transfer to the nonhuman primate brain. Exp. Neurol. 160:1-16.
    • 8. Taylor, R.M., and Wolfe, J.H. 1997. Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase. Nat. Med. 3:771-774.
    • 9. Bachoud-Levi, A.C., et al. 2000. Neuroprotective gene therapy for Huntington's disease using a polymer encapsulated BHK cell line engineered to secrete human CNTF. Hum. Gene Ther. 11:1723-1729.
    • 10. Hickey, W.F., Vass, K., and Lassmann, H. 1992. Bone marrow-derived elements in the central nervous system: an immunohistochemical and ultrastructural survey of rat chimeras. J. Neuropathol. Exp. Neurol. 51:246-256.
    • 11. Brazelton, T.R., Rossi, F.M.V., Keshet, G.I., and Blau, H.M. 2000. From marrow to brain: expression of neuronal phenotypes in adult mice. Science. 290:1775-1779.
    • 12. Mezey, E., Chandross, K.J., Harta, G., Maki, R.A., and McKercher, S.R. 2000. Turning blood into brain: cells bearing neuronal antigens generated in vivo from bone marrow. Science. 290:1779-1782.
    • 13. Mezey, E., et al. 2003. Transplanted bone marrow generates new neurons in human brains. Proc. Natl. Acad. Sci. U. S. A. 100:1364-1369.
    • 14. Weimann, J.M., Charlton, C.A., Brazelton, T., Hackman, R.C., and Blau, H.M. 2003. Contribution of transplanted bone marrow cells to Purkinje cells in human adult brains. Proc. Natl. Acad. Sci. U. S. A. 100:2088-2093.
    • 15. Eglitis, M.A., and Mezey, E. 1997. Hematopoietic cells differentiate into both microglia and macroglia in the brains of adult mice. Proc. Natl. Acad. Sci. U. S. A. 94:4080-4085.
    • 16. Kennedy, D.W., and Abkowitz, J.L. 1997. Kinetics of central nervous system microglial and macrophage engraftment. Analysis using a transgenic bone marrow transplantation model. Blood. 90:986-993.
    • 17. Priller, J., et al. 2001. Targeting gene-modified hematopoietic cells to the central nervous system: use of green fluorescent protein uncovers microglial engraftment. Nat. Med. 7:1356-1361.
    • 18. Krivit, W., Aubourg, P., Shapiro, E., and Peters, C. 1999. Bone marrow transplantation for globoid cell leukodystrophy, adrenoleukodystrophy, metachromatic leukodystrophy, and Hurler syndrome. Curr. Opin. Hematol. 6:377-382.
    • 19. Peters, C., and Steward, C.G. 2003. Hematopoietic cell transplantation for inherited metabolic diseases: an overview of outcomes and practice guidelines. Bone Marrow Transplant. 31:229-239.
    • 20. Krivit, W., Sung, J.H., Shapiro, E.G., and Lockman, L.A. 1995. Microglia: the effector cell for reconstitution of the central nervous system following bone marrow transplantation for lysosomal and peroxisomal storage diseases. Cell Transplant. 4:385-392.
    • 21. Neufeld, E.F., and Muenzer, J. 2001. Lysosomal storage disorders. In The metabolic and molecular bases of inherited disease. C.R. Scriver, A.L. Beaudet, W.S. Sly, and D. Valle, editors. McGraw-Hill. New York, New York, USA. 3421-3452.
    • 22. Ailles, L., et al. 2002. Molecular evidence of lentiviral vector-mediated gene transfer into human self-renewing, multi-potent, long-term NOD/SCID repopulating hematopoietic cells. Mol. Ther. 6:615-626.
    • 23. Guenechea, G., Gan, O.I., Dorrell, C., and Dick, J.E. 2001. Distinct classes of human stem cells that differ in proliferative and self-renewal potential. Nat. Immunol. 2:75-82.
    • 24. Miyoshi, H., Smith, K.A., Mosier, D.E., Verma, I.M., and Torbett, B.E. 1999. Transduction of human CD34+ cells that mediate long-term engraftment of NOD/SCID mice by HIV vectors. Science. 283:682-686.
    • 25. Hess, B., et al. 1996. Phenotype of arylsulfatase A-deficient mice: relationships to human metachromatic leukodystrophy. Proc. Natl. Acad. Sci. U. S. A. 93:14821-14826.
    • 26. Follenzi, A., Ailles, L.E., Bakovic, S., Geuna, M., and Naldini, L. 2000. Gene transfer by lentiviral vectors is limited by nuclear translocation and rescued by HIV-1 pol sequences. Nat. Genet. 25:217-222.
    • 27. Follenzi, A., and Naldini, L. 2002. HIV-based vectors. Preparation and use. Methods Mol. Med. 69:259-274.
    • 28. De Palma, M., and Naldini, L. 2002. Transduction of a gene expression cassette using advanced generation lentiviral vectors. Methods Enzymol. 346:514-529.
    • 29. Marchesini, S., et al. 1990. Synthesis, spectral properties and enzymatic hydrolysis of fluorescent derivatives of cerebroside sulfate containing long-wavelength-emission probes. Chem. Phys. Lipids. 53:165-175.
    • 30. Marchesini, S., Viani, P., Cestaro, B., and Gatt, S. 1989. Synthesis of pyrene derivatives of cerebroside sulfate and their use for determining arylsulfatase A activity. Biochim. Biophys. Acta. 1002:20-27.
    • 31. De Palma, M., Venneri, M.A., Roca, C., and Naldini, L. 2003. Targeting exogenous genes to tumor angiogenesis by transplantation of genetically modified hematopoietic stem cells. Nat. Med. 9:789-795.
    • 32. Santambrogio, L., et al. 2001. Developmental plasticity of CNS microglia. Proc. Natl. Acad. Sci. U. S. A. 98:6295-6300.
    • 33. Ohmi, K., et al. 2003. Activated microglia in cortex of mouse models of mucopolysaccharidoses I and IIIB. Proc. Natl. Acad. Sci. U. S. A. 100:1902-1907.
    • 34. Crawley, J.N. 2000. What's wrong with my mouse? John Wiley and Sons Ltd. New York, New York, USA. 47-63.
    • 35. Westerhof, G.R., et al. 2000. Comparison of different busulfan analogues for depletion of hematopoietic stem cells and promotion of donor-type chimerism in murine bone marrow transplant recipients. Cancer Res. 60:5470-5478.
    • 36. Rezaie, P., and Male, D. 2002. Mesoglia & microglia: a historical review of the concept of mononuclear phagocytes within the central nervous system. J. Hist. Neurosci. 11:325-374.
    • 37. Hickey, W.F., and Kimura, H. 1988. Perivascular microglial cells of the CNS are bone marrow-derived and present antigen in vivo. Science. 239:290-292.
    • 38. Tonra, J.R., et al. 2001. Comparison of the timing of acute blood-brain barrier breakdown to rabbit immunoglobulin G in the cerebellum and spinal cord of mice with experimental autoimmune encephalomyelitis. J. Comp. Neurol. 29:131-144.
    • 39. Bruck, W. 1997. The role of macrophages in Wallerian degeneration. Brain Pathol. 7:741-752.
    • 40. Mueller, M., et al. 2001. Rapid response to identified resident endoneurial macrophages to nerve injury. Am. J. Pathol. 159:2187-2197.
    • 41. Kuhlmann, T., et al. 2002. Differential regulation of myelin phagocytosis by macrophages/microglia, involvement of target myelin, Fc receptors and activation by intravenous immunoglobulins. J. Neurosci. Res. 67:185-190.
    • 42. Kreutzberg, G.W. 1996. Microglia: a sensor for pathological events in the CNS. Trends Neurosci. 19:312-318.
    • 43. Mueller, M., et al. 2003. Macrophage response to peripheral nerve injury: the quantitative contribution of resident and hematogenous macrophages. Lab. Invest. 83:175-185.
    • 44. Wada, R., Tifft, C.J., and Proia, R.L. 2000. Microglial activation precedes acute neurodegeneration in Sandhoff disease and is suppressed by bone marrow transplantation. Proc. Natl. Acad. Sci. U. S. A. 97:10954-10959.
    • 45. Sangalli, A., et al. 1998. Transduced fibroblasts and metachromatic leukodystrophy lymphocytes transfer arylsulphatase A to myelinating glia and deficient cells in vitro. Hum. Gene Ther. 9:2111-2119.
    • 46. Muschol, N., et al. 2002. Secretion of phosphomannosyl-deficient arylsulphatase A and cathepsin D from isolated human macrophages. Biochem. J. 368:845-853.
    • 47. Matzner, U., Harzer, K., Learish, R.D., Barranger, J.A., and Gieselmann, V. 2000. Long-term expression and transfer of arylsulfatase A into brain of arylsulfatase A-deficient mice transplanted with bone marrow expressing the arylsulfatase A cDNA from a retroviral vector. Gene Ther. 7:1250-1257.
    • 48. Matzner, U., et al. 2001. Bone marrow stem cell gene therapy of arylsulfatase A-deficient mice, using an arylsulfatase A mutant that is hypersecreted from retrovirally transduced donor-type cells. Hum. Gene Ther. 12:1021-1033.
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